Sionna Therapeutics, Inc. (Nasdaq: SION), a clinical-stage biopharmaceutical company on a mission to revolutionize the current treatment paradigm for cystic fibrosis (CF), today announced the ...
A national study showed decreasing mortality for cystic fibrosis but increasing mortality for sickle cell disease from 2008 to 2023. The trends affected nearly all age groups. The researchers ...
Cystic fibrosis is among the most common, known and studied genetic diseases. It affects over 100,000 people worldwide and ...
The gene editing treatment targets the relatively common 1717-1G>A splicing mutation, which does not respond to many current CF therapies.
Add Yahoo as a preferred source to see more of our stories on Google. The genetic disorder cystic fibrosis is unique because it can cause both breathing and digestive problems. Some 40,000 people in ...
In children with cystic fibrosis, the initiation of elexacaftor-tezacaftor-ivacaftor therapy may alter the status of fat soluble vitamins and change how supplementation relates to their serum levels.
An expensive drug hailed as life-changing for people with a rare strain of cystic fibrosis is a step closer to being available to people in Nova Scotia. Before now, Kalydeco was selling for roughly ...
The Megan’s Wish live auction for cystic fibrosis is set for May 9 at the National Guard Armory, 1925 First Ave., Seymour.
The local Cystic Fibrosis organisation has lost one of its great supporters and fundraisers following the recent death of ...
For roughly one in ten people living with cystic fibrosis, the drugs that have transformed survival for most CF patients are ...