Healio

Luxturna shows long-term maintenance of ambulatory vision, visual field

Please provide your email address to receive an email when new articles are posted on . Luxturna maintained long-term improvements in ambulatory vision, light sensitivity and visual field in patients ...
Nasdaq

Spark Therapeutics Wins Prix Galien USA Award for LUXTURNA® (voretigene neparvovec-rzyl) as Best Biotechnology Product

PHILADELPHIA, Oct. 25, 2019 (GLOBE NEWSWIRE) -- Spark Therapeutics (NASDAQ:ONCE), a fully integrated, commercial gene therapy company dedicated to challenging the inevitability of genetic disease, ...
Healio

Study investigates safety, efficacy of Luxturna in real-world clinical practice

Please provide your email address to receive an email when new articles are posted on . Initial findings from the real-world PERCEIVE study of voretigene neparvovec in patients with RPE65 ...
BioWorld

Spark plug: Luxturna green-lighted to treat rare RPE65-associated vision loss

BioWorld - Sunday, October 15, 2023 See today's BioWorld Home » Spark plug: Luxturna green-lighted to treat rare RPE65-associated vision loss Subscribe to BioWorld™ news services See subscription ...
Kaleido Scope

UAB Callahan Eye Is the Newest Site for Gene Therapy Treatment

UAB Callahan Eye has been named the newest site for Spark Therapeutics’ Luxturna, the first FDA-approved gene therapy treatment for those diagnosed with Leber Congenital Amaurosis(LCA). LCA is a ...
The American Journal of Managed Care

Voretigene Neparvovec Helps Patients With RPE65-Related Retinopathy Regain Bilateral Function

Voretigene neparvovec-rzyl (VN) therapy partially restored electroretinogram (ERG) responses in some RPE65-related retinopathy patients, with sustained improvements over several years. The study ...
Medscape

FDA Approves Novel Gene Therapy for Rare Form of Vision Loss

The US Food and Drug Administration (FDA) today approved a new gene therapy to treat a rare form of inherited vision loss that can lead to blindness. Voretigene neparvovec-rzyl (Luxturna, Spark ...
The American Journal of Managed Care

Team Creates Algorithm to Allocate Gene Therapy for Patients With Inherited Vision Loss

The development of a successful gene therapy for RPE65-associated inherited retinal disease is a major breakthrough, but it also prompts difficult questions about which patients are good candidates ...
Kaleido Scope

UAB Callahan Eye Hospital offering new gene therapy treatment for an inherited retinal disease

It is a prescription gene therapy used for the treatment of patients with inherited retinal disease due to mutations in both copies of the RPE65 gene, which can only be confirmed through genetic ...
Forbes

Eye-Catching Innovations: Gene Therapies For Retinal Disorders

This story is part of a series on the current progression in Regenerative Medicine. This piece is part of a series dedicated to the eye and improvements in restoring vision. In 1999, I defined ...
GEN

The Italian Job: An Interview with Gene Therapist Federico Mingozzi

The Chief Scientific Officer of Spark Therapeutics, Federico Mingozzi, surveys the hopes and challenges facing the human gene therapy community. After a distinguished career in academic medicine, ...