FDA approves first treatment for rare blood disorder in pediatric patients 12 and older

The treatment for acquired thrombotic thrombocytopenic purpura, a rare blood disorder that causes blood clots in the small ...
The Cardiology Advisor

Cablivi Approved for Pediatric Acquired Thrombotic Thrombocytopenic Purpura

The FDA expanded the approval of Cablivi to include pediatric patients 12 years and older with acquired thrombotic thrombocytopenic purpura.
MedPage Today

Eltrombopag Improves Outcomes in Kids With Newly Diagnosed ITP

SAN DIEGO -- Treatment with eltrombopag (Promacta) for pediatric patients with newly diagnosed immune thrombocytopenia (ITP) led to a significantly higher rate of durable platelet response compared ...
WebMD

How Nplate Works for Immune Thrombocytopenia (ITP)

How Does It Work for ITP? There is no cure for ITP. Its symptoms can vary from person to person, with some people not having any symptoms. Because ITP causes low platelets, the main side effects that ...
MPR

FDA Clears Yartemlea for HSCT-Associated Thrombotic Microangiopathy

The Food and Drug Administration has approved Yartemlea ® (narsoplimab-wuug) for the treatment of adult and pediatric patients aged 2 years and older with hematopoietic stem cell transplant ...
ascopubs.org

Whole-Genome Profiling of Pediatric Diffuse Intrinsic Pontine Gliomas Highlights Platelet-Derived Growth Factor Receptor α and Poly (ADP-ribose) Polymerase As Potential ...

Phase II, Randomized, Open-Label Study of Pegfilgrastim-Supported VDC/IE Chemotherapy in Pediatric Sarcoma Patients Diffuse intrinsic pontine glioma (DIPG) is one of the most devastating of pediatric ...