A drug used to treat one inborn error of metabolism may be effective against another, according to a study published online March 6 in Science Translational Medicine ...

PRINCETON, N.J., Oct. 26, 2023 (GLOBE NEWSWIRE) -- Medunik USA (member of Duchesnay Pharmaceutical Group, an international company selected in the Government of Canada's first Global Hypergrowth ...

MALVERN, Pa., Oct. 20, 2025 /PRNewswire/ -- Endo, a wholly-owned subsidiary of Mallinckrodt plc, announced today the launch of a generic version of Amgen's RAVICTI® (glycerol phenylbutyrate), 1.1 ...

This medication is used along with diet changes for long-term treatment of a certain inherited disorder (urea cycle disorder). Sodium phenylbutyrate helps remove a certain chemical (ammonia) from the ...

Evaluation of a 7-Day Continuous Intravenous Infusion of Decitabine: Inhibition of Promoter-Specific and Global Genomic DNA Methylation Pharmacokinetic data were obtained from two trials involving ...

This medication is a nitrogen-binding agent, prescribed for the treatment of Urea Cycle Disorders (UCD) in pediatric patients more than 2 years old and adults.

SOUTH SAN FRANCISCO, Calif.--(BUSINESS WIRE)-- Hyperion Therapeutics, Inc. today announced that the Company’s phase III pivotal study of glycerol phenylbutyrate (HPN-100), an investigational drug for ...

Review the side-effects of Glycerol Phenylbutyrate as documented in medical literature. The term "side effects" refers to unintended effects that can occur as a result of taking the medication. In ...

September 7, 2007 — The US Food and Drug Administration (FDA) has granted orphan drug designation for sodium phenylbutyrate for the treatment of spinal muscular atrophy, MGCD0103 for the treatment of ...

DUBLIN--(BUSINESS WIRE)--Horizon Pharma plc (NASDAQ: HZNP) today announced the U.S. Food and Drug Administration (FDA) has approved a supplemental new drug application (sNDA) to expand the age range ...

Benzoate and phenylbutyrate are widely used in the treatment of urea cycle disorders, but detailed studies on pharmacokinetics and comparative efficacy on nitrogen excretion are lacking.