A one-time gene-editing therapy, exagamglogene autotemcel (exa-cel), has demonstrated sustained and clinically meaningful ...

CHICAGO (WLS) -- Sickle cell anemia disproportionately affects Black people, causing severe pain, potential organ damage and in some cases, death. Many times, only blood transfusions can provide ...

An increasing demand for gene therapies is focusing the industry on enhancing production capabilities, transitioning from ...

(InvestigateTV) — A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis. In 2023, the FDA approved Lyfgenia, developed by ...

Vertex Pharmaceuticals Inc. (($VRTX)) announced an update on their ongoing clinical study. Vertex Pharmaceuticals Inc. is conducting a Phase 3 ...

At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...

Life expectancy has soared and interest in the disease is growing, but breakthrough gene therapies are extraordinarily ...